What should we expect when taking part in a clinical trial?
Deciding to be part of a clinical trial may be a new experience — both exciting and at times overwhelming. While each trial and every family's experience in a trial is different, there are some common elements many patients and their families should consider.
Tests in Duchenne muscular dystrophy trials
In addition to physical exams, blood draws, scans, and interviews, Duchenne trials may have a variety of other tests, such as those that measure muscle strength and endurance.
Common measurements used in clinical trials for Duchenne:
Interpreting test scores
While every child with Duchenne is unique, by looking at the results in a group of treated children and comparing those results with children who have not been treated, doctors may be able to see whether the medicine is working.